An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...

Advances delivered what may feel like medical miracles, including the first bladder transplant, a lifesaving personalized ...

For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...

Huntington's Disease burdens caregivers in India, facing financial strain and limited support amid widespread underdiagnosis ...

UCI’s $12M CIRM award for hNSC-01 marks a pivotal shift to clinical-stage development. See how this state-funded "bridge" is ...

Huntington's disease (HD) is a hereditary neurodegenerative disorder caused by a mutation in the gene called huntingtin on chromosome 4. HD is inherited in an autosomal dominant fashion, so that each ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

Researchers have implicated a new gene in the progression of Huntington's disease in a brain organoid model. The gene may contribute to brain abnormalities much earlier than previously thought. Six ...

New York, USA, June 03, 2025 (GLOBE NEWSWIRE) -- Huntington’s Disease Clinical Trial Pipeline Analysis: 20+ Key Companies Shaping the Future of Dopamine Receptor Antagonists Therapeutics | ...

An experimental gene therapy has become the first treatment to successfully slow the progression of Huntington’s disease. While the findings are still preliminary, the approach could be a major ...

In many respects, Huntington’s disease is the epitome of a well-understood hereditary disease. The condition was comprehensively described almost a century and a half ago 1. Its symptoms are ...

Elli Hofmeister started to lag behind in school when she was 8 years old. By the age of 9, she needed an extra hour of tutoring each night to keep up. Elli’s family chalked up her problems to a ...