A gene-editing therapy may correct a defect in the DYSF gene that drives a form of limb-girdle muscular dystrophy (LGMD), per ...

Columnist Shalom Lim saw elements of his own journey with DMD reflected in the Netflix documentary "The Remarkable Life of ...

Capricor's biologics license application for deramiocel (CAP-1002) is draws largely on the Phase 2 HOPE-2 trial and its ...

Muscular Dystrophy News Today covered the latest studies, treatment advances, and clinical trials for different types of the ...

Caregiving for young men with Duchenne isn't easy, but columnist Betty Vertin and her husband have learned to provide care as a team.

In the past 12 months, our oldest daughter got married, our oldest son moved across town into a college dorm, another son started his final year of high school, and, most significantly, I returned to ...

Living with Duchenne muscular dystrophy (DMD) has involved a series of challenges and triumphs, each shaping the person I am today. As 2025 approaches, I’m reflecting on that journey as well as ...

Agamree (vamorolone) has been recommended for use in the National Health Service (NHS) in England, Wales, and Northern Ireland for treating Duchenne muscular dystrophy (DMD) patients, 4 and older. “We ...

The Muscular Dystrophy Association (MDA) has awarded nearly two dozen new grants to fund research into various forms of muscular dystrophy, including Duchenne and limb-girdle, as well as related ...